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NVS-SM2
an activator of pre-mRNA splicing
Also Known As:
2-(6-(methyl(2,2,6,6-tetramethylpiperidin-4-yl)amino)-pyridazin-3-yl)-5-(1H-pyrazol-4-yl)phenol
Networked:
1
relevant articles (
0
outcomes,
0
trials/studies)
Bio-Agent Context: Research Results
Heterocyclic Compounds: 198
1-Ring Heterocyclic Compounds
Azoles: 2138
Pyrazoles: 61
NVS-SM2: 1
Piperidines: 17
NVS-SM2: 1
Pyridazines: 11
NVS-SM2: 1
Experts
1.
Abou-Hamdan, Hussein
: 1 article (01/2018)
2.
Désaubry, Laurent
: 1 article (01/2018)
Related Diseases
1.
Spinal Muscular Atrophy (Progressive Muscular Atrophy)
01/01/2018 - "
NVS-SM2, the first activator of pre-mRNA splicing, displays remarkable pharmacological in vivo activities in models of spinal muscular atrophy.
"
Related Drugs and Biologics
1.
RNA Precursors (Precursor, mRNA)